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D-Bifunctional Protein Deficiency

Disease ID: disease_node_17502

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DbxrefGARD:4539, ICD10CM:E71.3, MIM:261515, ORDO:300
SubclassofDOID_906
Data SourceDOID
Doid LabelD-bifunctional protein deficiency
Doid DescriptionA peroxisomal disease characterized by, in severe cases, infantile-onset of hypotonia, seizures, and abnormal facial features with most dying before age 2 years that has_material_basis_in homozygous or compound heterozygous mutation in the HSD17B4 gene on chromosome 5q2.
Disease Node Iddisease_node_17502
Doid IdDOID_0090031
Disease Has Basis InSO_0001537
LabelD-Bifunctional Protein Deficiency